111. Congenital myopathy Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 10 / Drugs : 17 - (DrugBank : 5) / Drug target gene : 1 - Drug target pathways : 9
Drugs and their primary sponsors and trial info
AT132
Audentes Therapeutics Inc.
2018 Phase 1;Phase 2 EUCTR2017-000876-27-FR France;Germany;United Kingdom;United States;
2018 Phase 1;Phase 2 EUCTR2017-000876-27-DE Canada;France;Germany;United Kingdom;United States;
2017 Phase 1;Phase 2 EUCTR2017-000876-27-GB France;Germany;United Kingdom;United States;
ApoTamox
James Dowling
2020 Phase 1/Phase 2 NCT04915846 Canada;United Kingdom;United States;
DYN101
Dynacure
2021 Phase 1/Phase 2 NCT04743557 France;Germany;
2020 Phase 1/Phase 2 NCT04033159 Belgium;Denmark;France;Germany;Netherlands;United Kingdom;United States;
- Phase 1;Phase 2 EUCTR2020-004608-32-DE France;Germany;Netherlands;Spain;
L-Tyrosine
Hadassah Medical Organization
2014 Phase 2 NCT02035501 Israel;
N-acetylcysteine
National Institute of Nursing Research (NINR)
2015 Phase 1/Phase 2 NCT02362425 United States;
RAAV8-Des-hMTM1
Audentes Therapeutics Inc.
2018 Phase 1;Phase 2 EUCTR2017-000876-27-FR France;Germany;United Kingdom;United States;
2018 Phase 1;Phase 2 EUCTR2017-000876-27-DE Canada;France;Germany;United Kingdom;United States;
2017 Phase 1;Phase 2 EUCTR2017-000876-27-GB France;Germany;United Kingdom;United States;
SALBUTAMOL SULFATE
Västra götalandsregionen
2020 Phase 4 EUCTR2019-001147-51-SE Sweden;
Salbutamol (as Salbutamol Sulfate) 2 Mg Oral Tablet
Vastra Gotaland Region
2021 - NCT05099107 Sweden;
Salbutamol Only Product in Oral Dose Form
Vastra Gotaland Region
2021 - NCT05099107 Sweden;
Ventoline oral solution 0,4mg/ml
Västra götalandsregionen
2020 Phase 4 EUCTR2019-001147-51-SE Sweden;
Ventoline tablet
Västra götalandsregionen
2020 Phase 4 EUCTR2019-001147-51-SE Sweden;
Audentes Therapeutics Inc.
2018 Phase 1;Phase 2 EUCTR2017-000876-27-FR France;Germany;United Kingdom;United States;
2018 Phase 1;Phase 2 EUCTR2017-000876-27-DE Canada;France;Germany;United Kingdom;United States;
2017 Phase 1;Phase 2 EUCTR2017-000876-27-GB France;Germany;United Kingdom;United States;
ApoTamox
James Dowling
2020 Phase 1/Phase 2 NCT04915846 Canada;United Kingdom;United States;
DYN101
Dynacure
2021 Phase 1/Phase 2 NCT04743557 France;Germany;
2020 Phase 1/Phase 2 NCT04033159 Belgium;Denmark;France;Germany;Netherlands;United Kingdom;United States;
- Phase 1;Phase 2 EUCTR2020-004608-32-DE France;Germany;Netherlands;Spain;
L-Tyrosine
Hadassah Medical Organization
2014 Phase 2 NCT02035501 Israel;
N-acetylcysteine
National Institute of Nursing Research (NINR)
2015 Phase 1/Phase 2 NCT02362425 United States;
RAAV8-Des-hMTM1
Audentes Therapeutics Inc.
2018 Phase 1;Phase 2 EUCTR2017-000876-27-FR France;Germany;United Kingdom;United States;
2018 Phase 1;Phase 2 EUCTR2017-000876-27-DE Canada;France;Germany;United Kingdom;United States;
2017 Phase 1;Phase 2 EUCTR2017-000876-27-GB France;Germany;United Kingdom;United States;
SALBUTAMOL SULFATE
Västra götalandsregionen
2020 Phase 4 EUCTR2019-001147-51-SE Sweden;
Salbutamol (as Salbutamol Sulfate) 2 Mg Oral Tablet
Vastra Gotaland Region
2021 - NCT05099107 Sweden;
Salbutamol Only Product in Oral Dose Form
Vastra Gotaland Region
2021 - NCT05099107 Sweden;
Ventoline oral solution 0,4mg/ml
Västra götalandsregionen
2020 Phase 4 EUCTR2019-001147-51-SE Sweden;
Ventoline tablet
Västra götalandsregionen
2020 Phase 4 EUCTR2019-001147-51-SE Sweden;