245. Propionic acidemia Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 13 / Drugs : 16 - (DrugBank : 3) / Drug target gene : 1 - Drug target pathways : 6
Drugs and their primary sponsors and trial info
BBP-671
CoA Therapeutics, Inc., a BridgeBio company
2021 Phase 1 NCT04836494 United States;
CX-016492
ModernaTX, Inc
2020 Phase 1;Phase 2 EUCTR2019-003529-36-GB Canada;United Kingdom;United States;
CX-017950
ModernaTX, Inc
2020 Phase 1;Phase 2 EUCTR2019-003529-36-GB Canada;United Kingdom;United States;
Carbaglu
Mendel Tuchman
2012 Phase 2 NCT01599286 United States;
Carglumic Acid (Carbaglu®)
National Taiwan University Hospital
2019 - NCT04284917 Taiwan;
Disodium citrate
Nicola Longo
2008 Phase 1 NCT00645879 United States;
Glutamine
Nicola Longo
2008 Phase 1 NCT00645879 United States;
HST5040
HemoShear Therapeutics
2021 Phase 2 NCT04732429 United States;
MRNA-3927
ModernaTX, Inc
2020 Phase 1;Phase 2 EUCTR2019-003529-36-GB Canada;United Kingdom;United States;
ModernaTX, Inc.
2021 Phase 1/Phase 2 NCT05130437 Canada;United Kingdom;United States;
2021 Phase 1/Phase 2 NCT04159103 Canada;United Kingdom;United States;
Ornithine alpha ketoglutarate
Nicola Longo
2008 Phase 1 NCT00645879 United States;
CoA Therapeutics, Inc., a BridgeBio company
2021 Phase 1 NCT04836494 United States;
CX-016492
ModernaTX, Inc
2020 Phase 1;Phase 2 EUCTR2019-003529-36-GB Canada;United Kingdom;United States;
CX-017950
ModernaTX, Inc
2020 Phase 1;Phase 2 EUCTR2019-003529-36-GB Canada;United Kingdom;United States;
Carbaglu
Mendel Tuchman
2012 Phase 2 NCT01599286 United States;
Carglumic Acid (Carbaglu®)
National Taiwan University Hospital
2019 - NCT04284917 Taiwan;
Disodium citrate
Nicola Longo
2008 Phase 1 NCT00645879 United States;
Glutamine
Nicola Longo
2008 Phase 1 NCT00645879 United States;
HST5040
HemoShear Therapeutics
2021 Phase 2 NCT04732429 United States;
MRNA-3927
ModernaTX, Inc
2020 Phase 1;Phase 2 EUCTR2019-003529-36-GB Canada;United Kingdom;United States;
ModernaTX, Inc.
2021 Phase 1/Phase 2 NCT05130437 Canada;United Kingdom;United States;
2021 Phase 1/Phase 2 NCT04159103 Canada;United Kingdom;United States;
Ornithine alpha ketoglutarate
Nicola Longo
2008 Phase 1 NCT00645879 United States;