3. Spinal muscular atrophy
179 clinical trials, 102 drugs (DrugBank: 26 drugs), 52 drug target genes, 78 drug target pathways
Other name(s) = "Myelopathic muscular atrophy", "SMA I", "Werdnig-Hoffman disease", "SMA II", "Dubowitz disease", "SMA III", "Kugelberg-Welander disease", "SMA IV"