256. Muscle glycogenosis
161 clinical trials,   114 drugs   (DrugBank: 23 drugs),   26 drug target genes,   106 drug target pathways

Searched query = "Muscle glycogenosis", "Muscular glycogenosis", "Muscle glycogen storage disease", "Muscular glycogen storage disease", "Glycogen storage disease type ... show all
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

Search in Page e.g. "Phase 3", "Not recruiting", "Japan"
1 trial found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04476550
(ClinicalTrials.gov)
November 1, 202026/2/2020Clinical Specimen Collection From Pompe Disease PatientsDeveloping a Potential Cure for Pompe Disease: Clinical Specimen Collection From Individuals With Pompe DiseasePompe DiseaseDrug: FilgrastimSerhat Gumrukcu, MD PhDFrida Therapeutics LLCRecruiting3 Years30 YearsAll12United States