DDrare: Database of Drug Development for Rare Diseases

Prevenar13 (DrugBank: -)

2 diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
19	ライソゾーム病	1
265	脂肪萎縮症	1

19. ライソゾーム病　［臨床試験数：784，薬物数：673（DrugBank：101），標的遺伝子数：68，標的パスウェイ数：184］

Searched query = "Lysosomal storage disease", "Lysosomal disease", "Gaucher disease", "Niemann-Pick disease", "Niemann-Pick type C", "GM1-gangliosidosis", "GM1-ganglio ... show all
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 784 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2015-004846-25-BE (EUCTR)	15/07/2016	30/03/2016	Anti-oxLDL IgM antibodies as a novel therapy for metabolic lipid diseases	Immunization against oxLDL in patients with lysosomal lipid diseases and associated metabolic disorders	Familial hypercholesterolemia Niemann-Pick disease type B (NPB)Niemann-Pick disease type C (NPC)Partial lipodystrophy in children and adults;Therapeutic area: Body processes [G] - Metabolic Phenomena [G03]	Trade Name: Prevenar13 Product Name: Prevenar13	Maastricht University	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes		Phase 4	Belgium

265. 脂肪萎縮症　［臨床試験数：109，薬物数：164（DrugBank：59），標的遺伝子数：26，標的パスウェイ数：94］

Searched query = "Lipodystrophy", "Berardinelli-Seip syndrome", "Lawrence syndrome", "Barraquer-Simons syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 109 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2015-004846-25-BE (EUCTR)	15/07/2016	30/03/2016	Anti-oxLDL IgM antibodies as a novel therapy for metabolic lipid diseases	Immunization against oxLDL in patients with lysosomal lipid diseases and associated metabolic disorders	Familial hypercholesterolemia Niemann-Pick disease type B (NPB)Niemann-Pick disease type C (NPC)Partial lipodystrophy in children and adults;Therapeutic area: Body processes [G] - Metabolic Phenomena [G03]	Trade Name: Prevenar13 Product Name: Prevenar13	Maastricht University	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes		Phase 4	Belgium