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Other: prospective observational registry    (DrugBank: -)

1 disease
告示番号疾患名（ページ内リンク）臨床試験数
3脊髄性筋萎縮症1

3. 脊髄性筋萎縮症　［臨床試験数：179，薬物数：102（DrugBank：26），標的遺伝子数：52，標的パスウェイ数：78］
Searched query = "Spinal muscular atrophy", "Myelopathic muscular atrophy", "SMA I", "Werdnig-Hoffman disease", "SMA II", "Dubowitz disease", "SMA III", "Kugelberg-Welander disease", "SMA IV"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 179 trial found
No.TrialIDDate_
enrollment		Date_
registration		Public_titleScientific_titleConditionInterventionPrimary_
sponsor		Secondary_
sponsor		Recruitment_
Status		Inclusion_
agemin		Inclusion_
agemax		Inclusion_
gender		Target_
size		PhaseCountries
1NCT04174157
(ClinicalTrials.gov)		September 25, 201812/9/2019Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)A Prospective, Long-Term Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)Spinal Muscular Atrophy (SMA)Other: Prospective observational registry;Drug: ZolgensmaAveXis, Inc.United BioSource, LLCRecruitingN/AN/AAll500United States;Israel