Rp-l401    (DrugBank: -)

1 disease
告示番号疾患名(ページ内リンク)臨床試験数
326大理石骨病1

326. 大理石骨病 [臨床試験数:20,薬物数:52(DrugBank:14),標的遺伝子数:16,標的パスウェイ数:78
Searched query = "Osteopetrosis"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 20 trial found
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PhaseCountries
1NCT04525352
(ClinicalTrials.gov)
October 202011/8/2020A Trial to Evaluate Safety and Efficacy of RP-L401-0120 in Subjects With Infantile Malignant OsteopetrosisA Phase I Clinical Trial for Gene Therapy in Infantile Malignant Osteopetrosis (IMO) to Evaluate the Safety and Preliminary Efficacy of Autologous CD34+ Enriched Cells Transduced With a LV Vector Encoding the TCIRG1 GeneInfantile Malignant OsteopetrosisBiological: RP-L401Rocket Pharmaceuticals Inc.NULLNot yet recruiting1 MonthN/AAll2Phase 1NULL