Saline solution for injection    (DrugBank: -)

1 disease
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease1

19. Lysosomal storage disease    [ 784 clinical trials,   673 drugs,   (DrugBank: 101 drugs),   68 drug target genes,   184 drug target pathways]
Searched query = "Lysosomal storage disease", "Lysosomal disease", "Gaucher disease", "Niemann-Pick disease", "Niemann-Pick type C", "GM1-gangliosidosis", "GM1-ganglio ... show all
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 784 trial found
No.TrialIDDate_
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Public_titleScientific_titleConditionInterventionPrimary_
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Inclusion_
agemin
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agemax
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PhaseCountries
1NCT03153319
(ClinicalTrials.gov)
June 5, 201711/5/2017Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I and IIPhase 1/2 Study of the Effect of Adalimumab on Physical Function and Musculoskeletal Disease in Mucopolysaccharidosis Types I and IIMucopolysaccharidosis I;Mucopolysaccharidosis IIDrug: Adalimumab Injection [Humira];Drug: Saline Solution for InjectionLundquist Institute for Biomedical Innovation at Harbor-UCLA Medical CenterNULLRecruiting5 YearsN/AAll14Phase 1;Phase 2United States