Home    Back

Hlb-001    (DrugBank: -)

1 disease
IDDisease name (Link within this page)Number of trials
246Methylmalonic acidemia1

246. Methylmalonic acidemia    [ 14 clinical trials,   22 drugs,   (DrugBank: 2 drugs),   1 drug target gene,   6 drug target pathways]
Searched query = "Methylmalonic acidemia"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 14 trial found
No.TrialIDDate_
enrollment		Date_
registration		Public_titleScientific_titleConditionInterventionPrimary_
sponsor		Secondary_
sponsor		Recruitment_
Status		Inclusion_
agemin		Inclusion_
agemax		Inclusion_
gender		Target_
size		PhaseCountries
1NCT04581785
(ClinicalTrials.gov)		January 15, 20212/10/2020Gene Therapy With hLB-001 in Pediatric Patients With Severe Methylmalonic AcidemiaA Phase 1/2 Open-label Clinical Study of hLB-001 Gene Therapy in Pediatric Patients With Methylmalonic Acidemia Characterized by MMUT MutationsMethylmalonic AcidemiaBiological: hLB-001LogicBio Therapeutics, Inc.NULLNot yet recruiting6 Months12 YearsAll8Phase 1;Phase 2United States