DDrare: Database of Drug Development for Rare Diseases

Procedure: total lymphoid irradiation (DrugBank: -)

3 diseases

ID	Disease name (Link within this page)	Number of trials
65	Primary immunodeficiency	1
284	Diamond-Blackfan anemia	1
326	Osteopetrosis	1

65. Primary immunodeficiency [ 413 clinical trials, 581 drugs, (DrugBank: 97 drugs), 68 drug target genes, 202 drug target pathways]

Searched query = "Primary immunodeficiency", "X-SCID", "Reticular dysgenesis", "Adenosine deaminase deficiency", "Omenn syndrome", "Purine nucleoside phosphorylase def ... show all
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 413 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00176878 (ClinicalTrials.gov)	June 2000	12/9/2005	Stem Cell Transplant for Bone Marrow Failure Syndromes	Bone Marrow Transplantation for Non-Malignant Congenital Bone Marrow Failure Disorders	Diamond-Blackfan Anemia;Kostmann's Neutropenia;Shwachman-Diamond Syndrome	Procedure: Stem cell transplant;Drug: Fludarabine monophosphate;Procedure: Total lymphoid irradiation;Drug: Busulfan;Biological: anti-thymocyte globulin	Masonic Cancer Center, University of Minnesota	NULL	Completed	N/A	35 Years	All	10	Phase 2;Phase 3	United States

284. Diamond-Blackfan anemia [ 37 clinical trials, 110 drugs, (DrugBank: 34 drugs), 22 drug target genes, 121 drug target pathways]

Searched query = "Diamond-Blackfan anemia"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 37 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00176878 (ClinicalTrials.gov)	June 2000	12/9/2005	Stem Cell Transplant for Bone Marrow Failure Syndromes	Bone Marrow Transplantation for Non-Malignant Congenital Bone Marrow Failure Disorders	Diamond-Blackfan Anemia;Kostmann's Neutropenia;Shwachman-Diamond Syndrome	Procedure: Stem cell transplant;Drug: Fludarabine monophosphate;Procedure: Total lymphoid irradiation;Drug: Busulfan;Biological: anti-thymocyte globulin	Masonic Cancer Center, University of Minnesota	NULL	Completed	N/A	35 Years	All	10	Phase 2;Phase 3	United States

326. Osteopetrosis [ 20 clinical trials, 52 drugs, (DrugBank: 14 drugs), 16 drug target genes, 78 drug target pathways]

Searched query = "Osteopetrosis"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 20 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00638820 (ClinicalTrials.gov)	September 2007	11/3/2008	Reduced Intensity AlloTransplant For Osteopetrosis	Reduced Intensity Allogeneic Transplantation For Severe Osteopetrosis Incorporating A Second Cd34 Selected Graft	Osteopetrosis	Procedure: Stem Cell or Umbilical Cord Blood Transplantation;Drug: Campath, Busulfan, Clofarabine;Procedure: Total Lymphoid Irradiation	Masonic Cancer Center, University of Minnesota	NULL	Terminated	N/A	45 Years	All	3	Phase 2	United States