Drug Description in Trials / DrugBank / KEGG DRUG /


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No. Drug (Description in trials) DrugBank KEGG DRUG KEGG GENES KEGG PATHWAY Disease ID
1291844----[2] 246, 299
2ATALUREN[1] Ataluren[1] D09323 --[6] 19, 113, 140, 246, 299, 329
3Ataluren 1000mg[1] Ataluren[1] D09323 --[1] 246
4Ataluren 125mg[1] Ataluren[1] D09323 --[1] 246
5Ataluren 250mg[1] Ataluren[1] D09323 --[1] 246
6BBP-671----[2] 245, 246
7Bucladesine[1] Bucladesine[1] D07546 [16] PDE10A,
PDE11A,
PDE1A,
PDE1B,
PDE1C,
PDE2A,
PDE3A,
PDE3B,
PDE4A,
PDE4B,
PDE4C,
PDE4D,
PDE7A,
PDE7B,
PDE8A,
PDE8B 💬
[18] Aldosterone synthesis and secretion, Apelin signaling pathway, Calcium signaling pathway, Cortisol synthesis and secretion, Cushing syndrome, Glucagon signaling pathway, Insulin signaling pathway, Metabolic pathways, Morphine addiction, Olfactory transduction, Parathyroid hormone synthesis, secretion and action, Progesterone-mediated oocyte maturation, Purine metabolism, Regulation of lipolysis in adipocytes, Renin secretion, Taste transduction, cAMP signaling pathway, cGMP-PKG signaling pathway 💬[1] 246
8Carbaglu[1] Carglumic acid[1] D07130 [1] CPS1 💬[6] Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism 💬[2] 245, 246
9Carglumic Acid[1] Carglumic acid[1] D07130 [1] CPS1 💬[6] Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism 💬[3] 245, 246, 251
10Carglumic Acid (Carbaglu®)[1] Carglumic acid[1] D07130 [1] CPS1 💬[6] Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism 💬[2] 245, 246
11Coenzyme A[1] Coenzyme A---[1] 246
12Compound 1a----[2] 246, 299
13HLB-001----[1] 246
14HST5040----[2] 245, 246
15Methylmalonyl-coenzyme A[2] (R)-methylmalonyl-CoA,
Coenzyme A
---[1] 246
16Modified mRNA encoding human methylmalonyl-coenzyme A mutase[2] (R)-methylmalonyl-CoA,
Coenzyme A
---[1] 246
17MRNA-3704----[1] 246
18MRNA-3705----[1] 246
19N-Carbamylglutamate[1] Carglumic acid[1] D07130 [1] CPS1 💬[6] Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism 💬[2] 245, 246
20None----[20] 6, 46, 51, 65, 66, 78, 84, 85, 96, 97, 140, 160, 161, 171, 222, 231, 246, 271, 299, 337
21PEG----[15] 6, 13, 41, 46, 60, 65, 78, 96, 97, 140, 144, 240, 246, 299, 337
22PTC-0161480----[2] 246, 299
23PTC-124----[2] 246, 299
24PTC-C124----[2] 246, 299
25PTC124----[4] 19, 113, 246, 299
26RhGH[1] Somatotropin---[6] 76, 78, 96, 193, 246, 337
27RPS 2505----[2] 246, 299
28Standard of Care Treatment----[3] 53, 245, 246