18. Spinocerebellar degeneration Clinical trials / Disease details
Clinical trials : 76 / Drugs : 98 - (DrugBank : 31) / Drug target genes : 44 - Drug target pathways : 65
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
1 | NCT02147886 (ClinicalTrials.gov) | July 2014 | 21/5/2014 | Study To Assess Safety, Tolerability and Efficacy of Intravenous Cabaletta in Patients With Machado-Joseph Disease | A Single-Center, Randomized, Double-Blind, Parallel-Group, Dose-Controlled Study, to Assess Safety, Tolerability and Efficacy of Intravenous Cabaletta® in Patients With Machado-Joseph Disease | Machado-Joseph Disease / Spinocerebellar Ataxia 3 | Drug: Cabaletta for IV infusion once weekly during 24 weeks | Bioblast Pharma Ltd. | NULL | Completed | 18 Years | 75 Years | Both | 15 | Phase 2 | Israel |