180. ATR-X syndrome Clinical trials / Disease details
Clinical trial : 1 / Drugs : 3 - (DrugBank : 2) / Drug target gene : 0 - Drug target pathway : 0
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | JPRN-jRCT2051220062 | 14/07/2022 | 14/07/2022 | Physician-initiated clinical trial in patients with 5-aminolevulinic acid-induced ATR-X syndrome. | Exploratory study to investigate the safety and efficacy of NPJ005 in patients with ATR-X syndrome. - IACT21003 | ATR-X syndrome infant, intellectual disability, epigenetics, guanine quadruplex;D008607 | Containing 5-aminolevulinic acid (5-ALA) hydrochloride and sodium ferrous citrate (SFC) Tablets (25 mg 5-ALA hydrochloride/39.2 mg SFC per tablet, NPJ005) for 24 weeks | Wada Takahito | NULL | Recruiting | >= 2age old | Not applicable | Male | 5 | Phase 2 | Japan |