19. Lysosomal storage disease Clinical trials / Disease details
Clinical trials : 899 / Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT00004454 (ClinicalTrials.gov) | October 1996 | 18/10/1999 | Phase I/II Study of Retroviral-Mediated Transfer of Iduronate-2-Sulfatase Gene Into Lymphocytes of Patients With Mucopolysaccharidosis II (Mild Hunter Syndrome) | Mucopolysaccharidosis II | Genetic: lymphocyte gene therapy | Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | University of Minnesota - Clinical and Translational Science Institute | Completed | 18 Years | N/A | Both | 2 | Phase 1/Phase 2 | United States |