244. Maple syrup urine disease Clinical trials / Disease details


Clinical trial : 1 Drug : 1 - (DrugBank : 1) / Drug target gene : 0 - Drug target pathway : 0

  
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agemin
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1NCT01529060
(ClinicalTrials.gov)
February 20136/2/2012Phenylbutyrate Therapy for Maple Syrup Urine DiseaseA Double-Blind, Randomized, Placebo-Controlled, Crossover Trial of Phenylbutyrate in the Treatment of Maple Syrup Urine DiseaseMaple Syrup Urine DiseaseDrug: Phenylbutyrate;Drug: Placebo powderBrendan LeeNULLCompleted3 YearsN/AAll20Phase 2/Phase 3United States