257. Hepatic glycogenosis Clinical trials / Disease details

Clinical trials : 14 / Drugs : 27 - (DrugBank : 7) / Drug target genes : 3 - Drug target pathways : 8

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2021-000903-19-IT (EUCTR)	14/12/2021	24/05/2021	A first-in-human study of UX053 in Patients with Glycogen Storage Disease type III (GSD III)	A Phase 1/2 First-in-human, 2-part Study to Evaluate the Safety, Tolerability, and Pharmacokinetics ...	Glycogen Storage Disease Type III (GSD III) MedDRA version: 20.1;Level: PT;Classification code 10053 ...	Product Name: mRNA che codifica l’enzima umano deramificante del glicogeno formulato in una nanopati ...	ULTRAGENYX PHARMACEUTICAL INC.	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	30	Phase 1;Phase 2	France;United States;Canada;Spain;Germany;United Kingdom;Italy

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