263. Cerebrotendinous xanthomatosis Clinical trials / Disease details


Clinical trials : 6 Drugs : 11 - (DrugBank : 2) / Drug target genes : 2 - Drug target pathways : 4

  
1 trial found
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1NCT04270682
(ClinicalTrials.gov)
January 31, 202012/2/2020Study to Evaluate Patients With Cerebrotendinous Xanthomatosis (RESTORE)A Phase 3 Study to Evaluate the Effects of Chenodeoxycholic Acid in Adult and Pediatric Patients With Cerebrotendinous XanthomatosisCTXDrug: Blinded CDCA 250 mg TID;Drug: Placebo;Drug: Open-Label CDCA 250 mg TID;Drug: Rescue Medication CDCA 250 mg TID;Drug: CDCA Weight-Based Dose TIDTravere Therapeutics, Inc.NULLRecruiting1 MonthN/AAll12Phase 3United States;Brazil