284. Diamond-Blackfan anemia Clinical trials / Disease details


Clinical trials : 36 Drugs : 95 - (DrugBank : 34) / Drug target genes : 23 - Drug target pathways : 126

  
1 trial found
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agemin
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1NCT02179359
(ClinicalTrials.gov)
September 2, 201427/6/2014Hematopoietic Stem Cell Transplant for High Risk HemoglobinopathiesMT2014-10C: Allogeneic Hematopoietic Stem Cell Transplant for Patients With High Risk Hemoglobinopathies and Other Red Cell Transfusion Dependent DisordersSickle Cell Disease;Transfusion Dependent Alpha- or Beta- Thalassemia;Diamond Blackfan Anemia;Paroxysmal Nocturnal Hemoglobinuria;Glanzmann Thrombasthenia;Severe Congenital Neutropenia;Shwachman-Diamond Syndrome;Non-Malignant Hematologic DisordersDrug: Reduced Toxicity Ablative Regimen;Drug: Reduced Intensity Preparative Regimen;Drug: Myeloablative Preparative RegimenMasonic Cancer Center, University of MinnesotaNULLRecruitingN/A55 YearsAll25N/AUnited States