TSHA-102 ( DrugBank: - )
1 disease
| ID | Disease name (Link within this page) | Number of trials |
|---|---|---|
| 156 | Rett syndrome | 1 |
156. Rett syndrome
Clinical trials : 44 / Drugs : 61 - (DrugBank : 23) / Drug target genes : 57 - Drug target pathways : 83
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT05606614 (ClinicalTrials.gov) | November 8, 2022 | 28/10/2022 | Safety and Efficacy of TSHA-102 in Adult Females With Rett Syndrome (REVEAL Adult Study) | Open-label, Randomized, Dose-escalation and Dose-expansion Study of the Safety and Preliminary Efficacy of a Single Intrathecal Administration of TSHA-102, an AAV9-Delivered Gene Therapy, in the Treatment of Adult Females With Rett Syndrome | Rett Syndrome | Genetic: TSHA-102 | Taysha Gene Therapies, Inc. | NULL | Recruiting | 18 Years | N/A | Female | 12 | Phase 1/Phase 2 | Canada |