Epithelial sheet generated from transduced autologous keratinocytes using pCCL-INVO-SP ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
160Congenital ichthyosis1

160. Congenital ichthyosis


Clinical trials : 42 Drugs : 71 - (DrugBank : 21) / Drug target genes : 18 - Drug target pathways : 112
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PhaseCountries
1EUCTR2011-003212-22-GB
(EUCTR)
03/06/201308/03/2013A clinical trial to study the effects of genetically modified patients' skin stem cellsPhase I study of ex-vivo lentiviral gene therapy for the inherited skin disease Netherton Syndrome - Gene Therapy for Netherton Syndrome Netherton Syndrome (NS)
MedDRA version: 14.1;Level: PT;Classification code 10062909;Term: Netherton's syndrome;System Organ Class: 10010331 - Congenital, familial and genetic disorders ;Therapeutic area: Diseases [C] - Skin and Connective Tissue Diseases [C17]
Product Name: Epithelial sheet generated from transduced autologous keratinocytes using pCCL-INVO-SP
INN or Proposed INN: epithelial sheet generated from transduced autologous keratinocytes using pCCL-INVO-SP
GOSH/ICH Joint Research & Development OfficeNULLNot Recruiting Female: yes
Male: yes
5 Human pharmacology (Phase 1): yes Therapeutic exploratory (Phase 2): no Therapeutic confirmatory - (Phase 3): no Therapeutic use (Phase 4): noUnited Kingdom