Transduced CD34+ hematopoietic stem cell ( DrugBank: - )
2 diseases
| ID | Disease name (Link within this page) | Number of trials |
|---|---|---|
| 19 | Lysosomal storage disease | 1 |
| 20 | Adrenoleukodystrophy | 1 |
19. Lysosomal storage disease
Clinical trials : 899 / Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT02559830 (ClinicalTrials.gov) | January 2015 | 12/8/2015 | Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy | A Phase I/II Clinical Trial of Lentiviral Hematopoietic Stem Cell Gene Therapy for Treatment of Developed Metachromatic Leukodystrophy and Adrenoleukodystrophy | Metachromatic Leukodystrophy;Adrenoleukodystrophy | Genetic: transduced CD34+ hematopoietic stem cell | Shenzhen Second People's Hospital | Shenzhen University;Guangzhou Women and Children's Medical Center | Recruiting | 1 Year | 16 Years | All | 50 | Phase 1/Phase 2 | China |
20. Adrenoleukodystrophy
Clinical trials : 61 / Drugs : 90 - (DrugBank : 31) / Drug target genes : 23 - Drug target pathways : 126
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT02559830 (ClinicalTrials.gov) | January 2015 | 12/8/2015 | Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy | A Phase I/II Clinical Trial of Lentiviral Hematopoietic Stem Cell Gene Therapy for Treatment of Developed Metachromatic Leukodystrophy and Adrenoleukodystrophy | Metachromatic Leukodystrophy;Adrenoleukodystrophy | Genetic: transduced CD34+ hematopoietic stem cell | Shenzhen Second People's Hospital | Shenzhen University;Guangzhou Women and Children's Medical Center | Recruiting | 1 Year | 16 Years | All | 50 | Phase 1/Phase 2 | China |