Hematopoetic Stem Cell Transplantation ( DrugBank: - )


5 diseases
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease1
65Primary immunodeficiency1
120Hereditary dystonia1
160Congenital ichthyosis1
326Osteopetrosis1

19. Lysosomal storage disease


Clinical trials : 899 Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182

65. Primary immunodeficiency


Clinical trials : 500 Drugs : 614 - (DrugBank : 119) / Drug target genes : 92 - Drug target pathways : 217

120. Hereditary dystonia


Clinical trials : 26 Drugs : 19 - (DrugBank : 3) / Drug target genes : 2 - Drug target pathways : 2

160. Congenital ichthyosis


Clinical trials : 42 Drugs : 71 - (DrugBank : 21) / Drug target genes : 18 - Drug target pathways : 112

326. Osteopetrosis


Clinical trials : 18 Drugs : 43 - (DrugBank : 14) / Drug target genes : 17 - Drug target pathways : 82