045251016 ( DrugBank: - )

1 disease

ID	Disease name (Link within this page)	Number of trials
19	Lysosomal storage disease	1

19. Lysosomal storage disease

Clinical trials : 899 / Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2018-002984-24-IT (EUCTR)	24/06/2020	21/10/2020	Study to Assess the Safety of Cystadrops® in Pediatric Cystinosis Patients from 6 Months to Less Tha ...	Open-label, Single-arm, Multicenter Study to Assess the Safety of Cystadrops® in Pediatric Cystinosi ...	Nephropatic Cystinosis patients with corneal cystine crystal deposits MedDRA version: 20.0;Level: LL ...	Trade Name: Cystadrops Product Name: Cystadrops Product Code: [045251016] INN or Proposed INN: Mercapta ...	Recordati Rare Diseases	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	5	Phase 3	France;Belgium;Germany;United Kingdom;Italy

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