GC1123 ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease1

19. Lysosomal storage disease


Clinical trials : 899 Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182
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agemin
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PhaseCountries
1NCT05422482
(ClinicalTrials.gov)
September 20, 202231/5/2022A Study to Evaluate the Safety, Tolerability, PK and PD of Intracerebroventricular GC1123 in Patients With MPS ?Phase 1, Open-Label, Ascending Dose Study to Evaluate the Safety, Tolerability, PK and PD of Intracerebroventricular GC1123 in Patients With MPS ? Who Have Central Nervous System Involvement and Are Receiving Treatment With Intravenous DrugMucopolysaccharidosis II;Hunter SyndromeBiological: GC1123GC Biopharma CorpNULLRecruiting18 Months18 YearsAll12Phase 1Korea, Republic of