Lymphocyte gene therapy ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease1

19. Lysosomal storage disease


Clinical trials : 899 Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182
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agemin
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PhaseCountries
1NCT00004454
(ClinicalTrials.gov)
October 199618/10/1999Phase I/II Study of Retroviral-Mediated Transfer of Iduronate-2-Sulfatase Gene Into Lymphocytes of Patients With Mucopolysaccharidosis II (Mild Hunter Syndrome)Mucopolysaccharidosis IIGenetic: lymphocyte gene therapyEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)University of Minnesota - Clinical and Translational Science InstituteCompleted18 YearsN/ABoth2Phase 1/Phase 2United States