ACTUS-101 ( DrugBank: - )
1 disease
| ID | Disease name (Link within this page) | Number of trials |
|---|---|---|
| 256 | Muscle glycogenosis | 1 |
256. Muscle glycogenosis
Clinical trials : 180 / Drugs : 133 - (DrugBank : 29) / Drug target genes : 25 - Drug target pathways : 105
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT03533673 (ClinicalTrials.gov) | December 17, 2018 | 13/4/2018 | AAV2/8-LSPhGAA (ACTUS-101) in Late-Onset Pompe Disease | A Phase 1 Study of the Safety of AAV2/8-LSPhGAA (ACTUS-101) in Late-onset Pompe Disease | Pompe Disease | Biological: ACTUS-101 | Asklepios Biopharmaceutical, Inc. | NULL | Recruiting | 18 Years | N/A | All | 13 | Phase 1/Phase 2 | United States |