Pegtarviliase ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
337Homocystinuria1

337. Homocystinuria


Clinical trials : 16 Drugs : 19 - (DrugBank : 7) / Drug target genes : 2 - Drug target pathways : 23
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agemin
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PhaseCountries
1NCT05154890
(ClinicalTrials.gov)
May 13, 202120/8/2021A Multiple Ascending Dose Study of ACN00177 (Pegtarviliase) in Subjects With CBS DeficiencyA Phase 1/2 Multiple Ascending-Dose Study in Subjects With Homocystinuria Due to Cystathionine ß-Synthase (CBS) Deficiency to Investigate the Safety, Pharmacokinetics, and Pharmacodynamics of ACN00177Homocystinuria Due to Cystathionine Beta-Synthase DeficiencyDrug: PegtarviliaseAeglea BiotherapeuticsNULLRecruiting12 YearsN/AAll36Phase 1/Phase 2United States;Australia;United Kingdom