AAV BBP-631 ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
81Congenital adrenal hyperplasia1

81. Congenital adrenal hyperplasia


Clinical trials : 87 Drugs : 87 - (DrugBank : 23) / Drug target genes : 12 - Drug target pathways : 68
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04783181
(ClinicalTrials.gov)
July 1, 20211/3/2021A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)A Phase 1/2, First-in-Human, Open-Label, Dose-Escalation Study of the Safety and Efficacy of Gene Therapy for Congenital Adrenal Hyperplasia Through Administration of an Adeno-Associated Virus (AAV) Serotype 5-Based Recombinant Vector Encoding the Human CYP21A2 GeneCongenital Adrenal HyperplasiaBiological: AAV BBP-631Adrenas Therapeutics IncNULLRecruiting18 YearsN/AAll25Phase 1/Phase 2United States;Australia