DDrare: Database of Drug Development for Rare Diseases

Cpx (DrugBank: -)

2 diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
215	ファロー四徴症	1
299	嚢胞性線維症	1

215. ファロー四徴症　［臨床試験数：19，薬物数：35（DrugBank：16），標的遺伝子数：16，標的パスウェイ数：47］

Searched query = "Tetralogy of Fallot", "Fallot tetralogy"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 19 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03835494 (ClinicalTrials.gov)	November 1, 2018	8/1/2019	Analysis of RV-Dysfunction in Fallot Patients	Tissue Doppler Imaging - A Promising Technique To Assess Myocardial Function In Adult Fallot Patients	Tetralogy of Fallot	Other: Transthoracic echocardiography at rest, during PLR, HG and CPX (including blood gas analysis in both groups). Additionally Fallot patients will undergo routine blood testings.	Klinik für Kardiologie, Pneumologie und Angiologie	NULL	Completed	18 Years	80 Years	All	60	N/A	Germany

299. 嚢胞性線維症　［臨床試験数：1,592，薬物数：1,539（DrugBank：255），標的遺伝子数：81，標的パスウェイ数：162］

Searched query = "Cystic fibrosis"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 1,592 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00004428 (ClinicalTrials.gov)	September 1997	18/10/1999	Phase I Randomized Study of CPX for the Treatment of Adult Patients With Mild Cystic Fibrosis		Cystic Fibrosis	Drug: CPX	FDA Office of Orphan Products Development	SciClone Pharmaceuticals	Completed	18 Years	N/A	Both	35	Phase 1	NULL