Orl-1b    (DrugBank: -)

1 disease
告示番号疾患名(ページ内リンク)臨床試験数
255複合カルボキシラーゼ欠損症1

255. 複合カルボキシラーゼ欠損症 [臨床試験数:1,薬物数:1(DrugBank:0),標的遺伝子数:0,標的パスウェイ数:0]
Searched query = "Multiple carboxylase deficiency", "Holocarboxylase synthetase deficiency", "HCS deficiency", "Biotinidase deficiency"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 1 trial found
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PhaseCountries
1NCT03269045
(ClinicalTrials.gov)
August 31, 201328/8/2017Study of ORL-1B in Patients With Biotinidase DeficiencyAn Open-label, Single-arm, Phase 2 Study of ORL-1B in Patients With Biotinidase DeficiencyBiotinidase DeficiencyDrug: ORL-1BOrpha LabsNULLCompletedN/A18 YearsAll20Phase 1;Phase 2NULL