DDrare: Database of Drug Development for Rare Diseases

Npi-001 (DrugBank: -)

2 diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
90	網膜色素変性症	1
303	アッシャー症候群	1

90. 網膜色素変性症　［臨床試験数：103，薬物数：158（DrugBank：42），標的遺伝子数：52，標的パスウェイ数：107］

Searched query = "Retinitis pigmentosa", "Rod dystrophy", "Rod-Cone Dystrophy"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 103 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04355689 (ClinicalTrials.gov)	September 3, 2020	17/4/2020	Safety and Efficacy of NPI-001 Tablets for RP Associated With Usher Syndrome	Safety and Efficacy of NPI-001 Tablets Versus Placebo for Treatment of Retinitis Pigmentosa Associated With Usher Syndrome	Usher Syndromes	Drug: NPI-001;Other: Placebo	Nacuity Pharmaceuticals, Inc.	Foundation Fighting Blindness	Recruiting	18 Years	N/A	All	48	Phase 1;Phase 2	Australia

303. アッシャー症候群　［臨床試験数：6，薬物数：11（DrugBank：0），標的遺伝子数：0，標的パスウェイ数：0］

Searched query = "Usher syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 6 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04355689 (ClinicalTrials.gov)	September 3, 2020	17/4/2020	Safety and Efficacy of NPI-001 Tablets for RP Associated With Usher Syndrome	Safety and Efficacy of NPI-001 Tablets Versus Placebo for Treatment of Retinitis Pigmentosa Associated With Usher Syndrome	Usher Syndromes	Drug: NPI-001;Other: Placebo	Nacuity Pharmaceuticals, Inc.	Foundation Fighting Blindness	Recruiting	18 Years	N/A	All	48	Phase 1;Phase 2	Australia