Device: mri without contrast agent injection    (DrugBank: -)

1 disease
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease1

19. Lysosomal storage disease    [ 784 clinical trials,   673 drugs,   (DrugBank: 101 drugs),   68 drug target genes,   184 drug target pathways]
Searched query = "Lysosomal storage disease", "Lysosomal disease", "Gaucher disease", "Niemann-Pick disease", "Niemann-Pick type C", "GM1-gangliosidosis", "GM1-ganglio ... show all
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 784 trial found
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PhaseCountries
1NCT03123523
(ClinicalTrials.gov)
October 18, 201612/4/2017Study of the Relation Between Lipid Myocardial Overload Evaluated by Cardiac Magnetic Resonance Imaging (MRI), Alteration of Longitudinal Myocardial Deformations by Echocardiography, and Clinical Achievements (Functional, Biological and Electrical) in Fabry Disease, and Its Outcomes.Fabry DiseaseDiagnostic Test: Echocardiography at T0;Diagnostic Test: Exercise test;Biological: Biological assays;Device: MRI with contrast agent injection;Device: MRI without contrast agent injection;Diagnostic Test: Echocardiography at M24University Hospital, BordeauxNULLRecruiting18 YearsN/AAll55N/AFrance