Enzyme replacement agent    (DrugBank: -)

1 disease
IDDisease name (Link within this page)Number of trials
256Muscle glycogenosis1

256. Muscle glycogenosis    [ 161 clinical trials,   114 drugs,   (DrugBank: 23 drugs),   26 drug target genes,   106 drug target pathways]
Searched query = "Muscle glycogenosis", "Muscular glycogenosis", "Muscle glycogen storage disease", "Muscular glycogen storage disease", "Glycogen storage disease type ... show all
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 161 trial found
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1NCT03045042
(ClinicalTrials.gov)
April 201727/1/2017Search for Serum/Plasma Biomarkers in Pompe's DiseaseSearch for Serum/Plasma Biomarkers in Pompe's DiseaseLate Onset Pompe Disease;Pompe DiseaseDrug: Enzyme Replacement AgentFundació Institut de Recerca de l'Hospital de la Santa Creu i Sant PauGenzyme, a Sanofi CompanyNot yet recruiting2 YearsN/AAll35N/ASpain