113. Muscular dystrophy Clinical trials / Disease details


Clinical trials : 622 Drugs : 485 - (DrugBank : 99) / Drug target genes : 59 - Drug target pathways : 168

  
1 trial found
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1NCT02376816
(ClinicalTrials.gov)
March 201526/2/2015Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular DystrophyPhase I Gene Transfer Clinical Trial for Duchenne Muscular Dystrophy Using rAAVrh74.MCK.Micro-dystrophinDuchenne Muscular DystrophyBiological: rAAVrh74.MCK.micro-DystrophinJerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)Completed7 YearsN/AMale2Phase 1United States