120. Hereditary dystonia Clinical trials / Disease details


Clinical trials : 25 Drugs : 21 - (DrugBank : 4) / Drug target genes : 2 - Drug target pathways : 2

  
1 trial found
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1NCT03570931
(ClinicalTrials.gov)
November 5, 201811/6/2018A Study to Assess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal DystrophyA Prospective Open-label Study to Assess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal DystrophyInfantile Neuroaxonal DystrophyDrug: RT001Retrotope, Inc.NULLActive, not recruiting18 Months10 YearsAll19Phase 2/Phase 3United States