171. Wilson disease Clinical trials / Disease details

Clinical trials : 68 / Drugs : 79 - (DrugBank : 17) / Drug target genes : 3 - Drug target pathways : 28

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04884815 (ClinicalTrials.gov)	September 27, 2021	7/5/2021	Clinical Study of UX701 AAV-Mediated Gene Transfer for the Treatment of Wilson Disease	A Randomized, Double-Blind, Placebo-Controlled, Multicenter, Seamless, Adaptive, Safety, Dose-Findin ...	Wilson Disease	Genetic: UX701;Other: Placebo;Drug: oral corticosteroids;Drug: Placebo for oral corticosteroids	Ultragenyx Pharmaceutical Inc	NULL	Recruiting	18 Years	N/A	All	90	Phase 1/Phase 2	United States

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