19. Lysosomal storage disease Clinical trials / Disease details
Clinical trials : 854 / Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT04453085 (ClinicalTrials.gov) | October 28, 2021 | 4/6/2020 | An Extension Study of JR-171-101 Study in Patients With MPS I | An Extension Study of JR-171-101 Study in Patients With Mucopolysaccharidosis Type I | Mucopolysaccharidosis I | Drug: JR-171 | JCR Pharmaceuticals Co., Ltd. | NULL | Recruiting | N/A | N/A | All | 15 | Phase 1/Phase 2 | Brazil;Japan |
| 2 | NCT04227600 (ClinicalTrials.gov) | September 1, 2020 | 27/12/2019 | A Study of JR-171 in Patients With Mucopolysaccharidosis I | Phase I/II Study of JR-171 ? Patients With Mucopolysaccharidosis Type I | Mucopolysaccharidosis I | Drug: JR-171 | JCR Pharmaceuticals Co., Ltd. | NULL | Recruiting | N/A | N/A | All | 19 | Phase 1/Phase 2 | United States;Brazil;Japan |