19. Lysosomal storage disease Clinical trials / Disease details


Clinical trials : 854 Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191

  
1 trial found
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agemin
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1NCT01614431
(ClinicalTrials.gov)
March 201119/5/2012N Acetyl Cysteine for Cystinosis PatientsN Acetyl Cysteine Can Decrease the Progression of Renal Disease in Cystinosis PatientsRenal Disease;CystinosisDrug: N acetyl cysteineUniversity of Sao PauloFundação de Amparo à Pesquisa do Estado de São PauloCompleted1 Year18 YearsBoth23Phase 4NULL