19. Lysosomal storage disease Clinical trials / Disease details

Clinical trials : 854 / Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191

2 trials found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2011-003685-32-ES (EUCTR)	27/01/2012	13/10/2011	NA	A Multicenter Extension Study of Taliglucerase alfa in Adult Subjects with Gaucher Disease - NA	Gaucher disease MedDRA version: 14.0;Level: PT;Classification code 10018048;Term: Gaucher's disease;System Organ Class: 10010331 - Congenital, familial and genetic disorders;Therapeutic area: Diseases [C] - Congenital, Hereditary, and Neonatal Diseases and Abnormalities [C16]	Product Name: recombinant human glucerebrosidase Product Code: Taliglucerase Alfa INN or Proposed INN: Taliglucerase alfa Other descriptive name: prGCD	Protalix Biotherapeutics	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	25		Serbia;Canada;Mexico;Chile;Spain;Italy;South Africa;Israel
2	EUCTR2011-003676-37-ES (EUCTR)	15/11/2011	14/09/2011	NA	A Multicenter Extension Study of Taliglucerase alfa in Pediatric Subjects with Gaucher Disease - NA	Gaucher disease MedDRA version: 14.0;Level: PT;Classification code 10018048;Term: Gaucher's disease;System Organ Class: 10010331 - Congenital, familial and genetic disorders;Therapeutic area: Diseases [C] - Congenital, Hereditary, and Neonatal Diseases and Abnormalities [C16]	Product Name: recombinant human glucerebrosidase Product Code: Taliglucerase Alfa INN or Proposed INN: Taliglucerase alfa Other descriptive name: prGCD	Protalix Biotherapeutics	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	15		Spain;South Africa;Israel