19. Lysosomal storage disease Clinical trials / Disease details


Clinical trials : 854 Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191

  
1 trial found
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agemin
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1NCT00418561
(ClinicalTrials.gov)
January 22, 20074/1/2007Metazym for the Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD)A Single Center, Open-label, Non-randomized, Uncontrolled, Multiple-dose, Dose Escalation Study of the Safety, Pharmacokinetics and Efficacy of Metazym for the Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD)Metachromatic Leukodystrophy (MLD)Biological: rhASA - Dose Level 1;Biological: rhASA - Dose Level 2;Biological: rhASA - Dose Level 3ShireNULLCompleted1 Year5 YearsAll13Phase 1Denmark