19. Lysosomal storage disease Clinical trials / Disease details


Clinical trials : 854 Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191

  
2 trials found
No.TrialIDDate_
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agemin
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PhaseCountries
1NCT01853852
(ClinicalTrials.gov)
September 201110/11/2011A Phase I, Randomized, Single-Blind, Four-Period Cross-Over, Placebo-Controlled, Dose-Escalation Study to Evaluate the Safety and Pharmacokinetics of Single Oral Doses of GR181413A/AT1001 in Healthy Japanese SubjectsA Phase I, Randomized, Single-Blind, Four-Period Cross-Over, Placebo-Controlled, Dose-Escalation Study to Evaluate the Safety and Pharmacokinetics of Single Oral Doses of GR181413A/AT1001 in Healthy Japanese SubjectsFabry DiseaseDrug: GR181413A/AT1001 solution;Drug: GR181413A/AT1001 capsule;Other: Potable water;Drug: Placebo capsuleAmicus TherapeuticsNULLCompleted20 Years55 YearsBoth14Phase 1Australia
2NCT00001972
(ClinicalTrials.gov)
September 199418/1/2000PET Scan of Brain Metabolism in Relation to Age and DiseasePositron Emission Tomography Imaging of Human Brain Phospholipid Metabolism in Relation to Age and DiseaseAlzheimer's Disease;Brain Neoplasm;Niemann Pick DiseaseDrug: 15 O WaterNational Institute of Neurological Disorders and Stroke (NINDS)NULLCompletedN/AN/ABoth123N/AUnited States