251. Urea cycle disorder Clinical trials / Disease details


Clinical trials : 48 Drugs : 52 - (DrugBank : 13) / Drug target genes : 4 - Drug target pathways : 29

  
1 trial found
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1JPRN-jRCTs041190055
24/07/201924/07/2019Carglumic Acid Administration for OTC DeficienscyA Clinical Study of Carglumic Acid in Patients with Late-Onset Ornithine Transcarbamylase Deficiency ornitine transcarbamylase deficiency patientsadministraton of carglumic acidIto TetsuyaNULLCompleteNot applicable< 75age oldBoth2Phase 4Japan