256. Muscle glycogenosis Clinical trials / Disease details


Clinical trials : 180 Drugs : 153 - (DrugBank : 30) / Drug target genes : 31 - Drug target pathways : 134

  
2 trials found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT01885936
(ClinicalTrials.gov)
June 201321/6/2013Safety and Efficacy of Albuterol in Individuals With Late-onset Pompe DiseaseA Phase 1/2 Double-Blind Study of the Safety and Efficacy of Albuterol on Motor Function in Individuals With Late-onset Pompe Disease Receiving Enzyme Replacement TherapyPompe DiseaseDrug: Albuterol;Drug: PlaceboDuke UniversityNULLCompleted18 YearsN/AAll16Phase 1/Phase 2United States
2NCT01859624
(ClinicalTrials.gov)
June 20128/5/2013Albuterol in Individuals With Late Onset Pompe Disease (LOPD)A Clinical Investigation of the Safety and Efficacy of Albuterol on Motor Function in Individuals With Late-onset Pompe Disease, Whether or Not Receiving Enzyme Replacement TherapyPompe DiseaseDrug: AlbuterolDuke UniversityNULLCompleted18 YearsN/AAll8Phase 1United States