284. Diamond-Blackfan anemia Clinical trials / Disease details


Clinical trials : 37 Drugs : 110 - (DrugBank : 34) / Drug target genes : 23 - Drug target pathways : 124

  
2 trials found
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1NCT00305708
(ClinicalTrials.gov)
August 200021/3/2006Busulfan, Antithymocyte Globulin, and Fludarabine Followed By a Donor Stem Cell Transplant in Treating Young Patients With Blood Disorders, Bone Marrow Disorders, Chronic Myelogenous Leukemia in First Chronic Phase, or Acute Myeloid Leukemia in First RemissionBone Marrow Stem Cell Transplantation for Children With Stem Cell Defects, Marrow Failure Syndromes, or Myeloid Leukemia in 1RemissionCongenital Amegakaryocytic Thrombocytopenia;Diamond-blackfan Anemia;Fanconi Anemia;Leukemia;Severe Congenital Neutropenia;ThrombocytopeniaBiological: anti-thymocyte globulin;Drug: busulfan;Drug: fludarabine phosphate;Procedure: allogeneic bone marrow transplantation;Procedure: peripheral blood stem cell transplantation;Procedure: umbilical cord blood transplantation;Radiation: radiation therapyUniversity of California, San FranciscoNational Cancer Institute (NCI)CompletedN/A17 YearsBoth40Phase 1/Phase 2United States
2NCT00001749
(ClinicalTrials.gov)
July 19983/11/1999Medical Treatment for Diamond Blackfan AnemiaTreatment of Diamond Blackfan Anemia With Antithymocyte Globulin and Cyclosporine AFanconi's Anemia;Hematologic DiseaseDrug: Antithymocyte globulin;Drug: CyclosporineNational Heart, Lung, and Blood Institute (NHLBI)NULLCompletedN/AN/ABoth25Phase 2United States