284. Diamond-Blackfan anemia Clinical trials / Disease details


Clinical trials : 37 Drugs : 110 - (DrugBank : 34) / Drug target genes : 23 - Drug target pathways : 124

  
1 trial found
No.TrialIDDate_
enrollment
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registration
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agemin
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agemax
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PhaseCountries
1NCT03966053
(ClinicalTrials.gov)
September 13, 201923/5/2019The Use of Trifluoperazine in Transfusion Dependent DBAPhase I/II, Open Label Study to Determine Safety of Trifluoperazine (TFP) in Adults With Red Blood Cell Transfusion-Dependent Diamond Blackfan AnemiaDiamond Blackfan Anemia;Pure Red Cell AplasiaDrug: TrifluoperazineAdrianna VlachosNULLTerminated18 Years65 YearsAll2Phase 1/Phase 2United States