285. Fanconi anemia Clinical trials / Disease details
Clinical trials : 59 / Drugs : 118 - (DrugBank : 32) / Drug target genes : 31 - Drug target pathways : 155
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
1 | NCT00243399 (ClinicalTrials.gov) | July 2004 | 20/10/2005 | Oxandrolone for the Treatment of Bone Marrow Aplasia in Fanconi Anemia | A Pilot Trial of Oxandrolone for the Treatment of Bone Marrow Aplasia in Patients With Fanconi Anemia | Fanconi Anemia | Drug: Oxandrolone | Children's Hospital Medical Center, Cincinnati | FDA Office of Orphan Products Development | Completed | N/A | N/A | Both | 10 | Phase 1 | United States |