285. Fanconi anemia Clinical trials / Disease details


Clinical trials : 59 Drugs : 118 - (DrugBank : 32) / Drug target genes : 31 - Drug target pathways : 155

  
1 trial found
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1NCT03609840
(ClinicalTrials.gov)
May 24, 20175/1/2018Study of Thiotepa and TEPA Drug Exposure in Pediatric Hematopoietic Stem Cell Transplant PatientsPopulation Pharmacokinetics and Pharmacodynamics of Thiotepa and TEPA in Pediatric Patients Undergoing Hematopoietic Cell Transplantation (HCT).Hematologic Malignancies;Nonmalignant Diseases;Immune Deficiency;Hemoglobinopathies;Genetic Inborn Errors of Metabolism;Fanconi Anemia;Thalassemia;Sickle Cell DiseaseDrug: ThiotepaUniversity of California, San FranciscoNULLActive, not recruitingN/A17 YearsAll25United States