3. Spinal muscular atrophy Clinical trials / Disease details


Clinical trials : 217 Drugs : 149 - (DrugBank : 33) / Drug target genes : 54 - Drug target pathways : 80

  
1 trial found
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agemin
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agemax
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1NCT02876094
(ClinicalTrials.gov)
January 29, 20199/8/2016Effect of Low-Dose Celecoxib on SMN2 in Patients With Spinal Muscular AtrophyA Pilot, Open-Label, Dose Response Study Investigating the Effect of Low-Dose Celecoxib on SMN2 in Patients With Spinal Muscular Atrophy (SMA)Spinal Muscular Atrophy (SMA)Drug: celecoxibHugh McMillanFamilies of Spinal Muscular Atrophy;Gwendolyn Strong FoundationTerminated2 Years80 YearsAll1Phase 2Canada