307. Canavan disease Clinical trials / Disease details

Clinical trials : 5 / Drugs : 9 - (DrugBank : 3) / Drug target genes : 2 - Drug target pathways : 2

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04833907 (ClinicalTrials.gov)	April 1, 2021	24/3/2021	rAAV-Olig001-ASPA Gene Therapy for Treatment of Children With Typical Canavan Disease	Phase 1/2, Open Label, Sequential Cohort Study of a Single Intracranial Dose of AVASPA Gene Therapy ...	Canavan Disease	Drug: rAAV-Olig001-ASPA;Drug: Levetiracetam;Drug: Prednisolone	Myrtelle Inc.	NULL	Recruiting	3 Months	60 Months	All	24	Phase 1/Phase 2	United States

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