310. Congenital anomalies syndrome Clinical trials / Disease details


Clinical trials : 10 Drugs : 18 - (DrugBank : 10) / Drug target genes : 3 - Drug target pathways : 7

  
1 trial found
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1NCT00064792
(ClinicalTrials.gov)
July 200311/7/2003Simvastatin Therapy in Smith-Lemli-Opitz SyndromeInvestigation of Simvastatin Therapy in Smith-Lemli-Opitz SyndromeSmith-Lemli-Opitz SyndromeDrug: Simvastatin Susp.;Drug: OraPlusForbes Porter, M.D.Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)Completed4 Years18 YearsAll23Phase 2United States